Rare disease definition
Examples of Rare disease in a sentence
Growth in the fourth quarter also benefited from the performance of the Rare disease (up 7.7%), Oncology (up 5.0%), CHC (up 4.6%) and Vaccines (up 7.8%) franchises.
The performance of multiple sclerosis (up 34.8%), Rare disease (up 4.5%) and CHC (up 9.5%) were offset by lower sales in Diabetes (down 5.6%), Established Rx Products (down 3.3%) and Vaccines (down 46.3%).
Rare disease patients have benefitted from the establishment of the ERNs. Repealing the Directive would remove the legal certainty the Directive’s objectives sought to provide.
Rare disease researchers often are, therefore, left to develop their own measures that have not been previously used or validated or they must modify existing measures developed for other disorders that may not provide the required sensitivity or specificity needed to accurately assess targeted outcomes.
Rare disease partnership: the role of the US HAEA in angioedema care.